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Breakthrough

Using gene transfer techniques pioneered by University of Florida faculty, Taiwanese doctors have restored some movement in four children bedridden with a rare, life-threatening neurological disease.

A Pioneer in Gene Therapy

The Powell Gene Therapy Center has been a pioneer in several ways:

  • Discovery of the unique life cycle of AAV (Dr. Kenneth Berns)
  • First use of AAV to deliver genes to cells in culture (Dr. Nicholas Muzyczka)
  • First use of AAV in animals and humans (Dr. Terry Flotte)
  • First use of AAV to in models of muscle and heart disease (Dr. Barry Byrne)
  • First use of AAV to reverse blindness in dogs with a genetic disease (Dr. Bill Hauswirth)
  • Active clinical trials in CF patients since 1996, including two that are currently enrolling patients (Dr. Terry Flotte)
  • A clinical trial in AAT deficiency (genetic emphysema) to begin in early 2004 (Drs. Terry Flotte and Mark Brantly)
  • The PGTC has competed successfully for federal funding in numerous arenas

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ChORD Half Marathon & 5K

August 13, 2014

Benefiting the Division of Genetics and Metabolism The race will support the Division of Genetics and Metabolism. Funds raised from the half marathon/5K will directly benefit the areas of greatest...

Dairy Queen donating to Shands two ways

August 13, 2014

UF Health Shands Children's Hospital will get a $200,000 donation from Dairy Queen, thanks to the help of the owners of some South Florida franchises.

Dairy Queen – Miracle Treat Day

August 13, 2014

Miracle Treat Day Thursday, August 14, 2014 Visit these participating locations near you and Dairy Queen will donate $1 or more from every Blizzard Treat sold to Children’s Miracle Network...

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